Systematic Review of Genetic Substrate Reduction Therapy in Lysosomal Storage Diseases: Opportunities, Challenges and Delivery Systems
ISSN: 1179-190X, 1173-8804
Year of publication: 2024
Volume: 38
Issue: 5
Pages: 657-680
Type: Review
ISSN: 1179-190X, 1173-8804
Year of publication: 2024
Volume: 38
Issue: 5
Pages: 657-680
Type: Review